Genetic activity underlies biological functions, so organisms have to make sure that the right genes are expressed at the ...
New POLARIS Phase I/II data presented at ASGCT show ETX101 gene therapy reducing seizures and improving neurodevelopment in children with SCN1A+ Dravet syndrome.
Researchers have identified a remarkably small but critical piece of genetic code that helps determine how brain cells connect, communicate, and function. The discovery not only deepens our ...
Researchers at Pohang University of Science and Technology (POSTECH) have built a platform that steers cell behavior using synthetic DNA produced inside cells, without making a single permanent change ...
A Moffitt Cancer Center researcher has introduced a new model that addresses one of biology's most fundamental questions: How ...
A new study reveals how transposable elements (TEs) expanded gene regulation during brain evolution, shaping modern neural development networks.
Researchers have developed a gene therapy that significantly slowed motor function loss in preclinical models of amyotrophic lateral sclerosis (ALS), offering new hope for treating the devastating ...
A treatment that targets dysfunctional photoreceptors regardless of the underlying genetic mutation leads to improved ...
A tiny switch in DNA allows neurons to change their function depending on the environment and alter behavior in worms.