The FDA’s Marty Makary and Vinay Prasad have laid out a path for CRISPR treatments on demand. An expert weighs in on what it ...

Globally there are just 805 people diagnosed with the rare PURA Syndrome, a neurodevelopmental disorder which causes developmental delay, decreased muscle tone and speech difficulties. Now researchers ...

Individuals with PURA Syndrome have been identified in the United Kingdom, Australia, Israel, Brazil, Spain, the Netherlands, France, Singapore, Hong Kong and Canada in addition to the United States.

Researchers at Victoria’s Florey Institute are working towards a global breakthrough in the treatment of a rare genetic disorder. Globally there are just 805 people diagnosed with the rare PURA ...