POLG-related diseases disrupt the function of the mitochondria, or "powerhouses" of the cell — starving them of energy.

For 21 years, Sebastien Beauzile lived with the chronic pain of sickle cell anemia.Now, thanks to a groundbreaking ge ...

NY resident Sebastien Beauzile was treated with a pioneering new gene therapy approach called Lyfgenia, curing his sickle cell anemia.

From STAT’s Andrew Joseph: AstraZeneca said this morning it was buying the Belgian cell therapy company EsoBiotec for $425 ...

In a nutshell Scientists discovered that an enzyme called SSAT1 turns helpful immune cells into harmful ones in psoriasis, ...

The Be Heard campaign will help patients with transportation which can be one of the biggest challenges to recovery.

Researchers from Columbia University and the German Cancer Center have found that stellate cells—star-shaped liver cells long ...

A stem cell therapy trial aimed at reducing neuroinflammation in patients with presymptomatic Alzheimer’s disease is underway ...

Researchers have revealed a new scientific clue that could unlock the key cellular pathway leading to devastating neurodegenerative diseases like Alzheimer's disease and amyotrophic lateral sclerosis ...

Sebastien Beauzile, 21, has been cured of sickle cell anemia, according to his doctors at Cohen Children’s Medical Center.

New findings show that the mitochondria powering our cells also control the ability of a DNA repair protein to suppress the senescence-associated secretory phenotype (SASP), which causes zombie-like ...

Sebastien Beauzile, 21, became the first person in New York state to be made symptom-free of sickle cell disease after ...