POLG-related diseases disrupt the function of the mitochondria, or "powerhouses" of the cell — starving them of energy.

For 21 years, Sebastien Beauzile lived with the chronic pain of sickle cell anemia.Now, thanks to a groundbreaking ge ...

NY resident Sebastien Beauzile was treated with a pioneering new gene therapy approach called Lyfgenia, curing his sickle cell anemia.

From STAT’s Andrew Joseph: AstraZeneca said this morning it was buying the Belgian cell therapy company EsoBiotec for $425 ...

The Be Heard campaign will help patients with transportation which can be one of the biggest challenges to recovery.

In a nutshell Scientists discovered that an enzyme called SSAT1 turns helpful immune cells into harmful ones in psoriasis, ...

A recently launched Phase 1 clinical trial is examining the safety and feasibility of a groundbreaking treatment approach for Parkinson's disease in which a patient's stem cells are reprogrammed to ...

A stem cell therapy trial aimed at reducing neuroinflammation in patients with presymptomatic Alzheimer’s disease is underway ...

Researchers have revealed a new scientific clue that could unlock the key cellular pathway leading to devastating neurodegenerative diseases like Alzheimer's disease and amyotrophic lateral sclerosis ...

Olga Rivera Ballesteros from the Center for Infectious Medicine (CIM) at the Department of Medicine, Huddinge (MedH) is ...

Sebastien Beauzile, 21, has been cured of sickle cell anemia, according to his doctors at Cohen Children’s Medical Center.